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Genetically Modified Adipose Tissue-Derived Stem/Stromal Cells, Using Simian Immunodeficiency Virus-Based Lentiviral Vectors, in the Treatment of Hemophilia B

Hemophilia is an X-linked bleeding disorder, and patients with hemophilia are deficient in a biologically active coagulation factor. This study was designed to combine the efficiency of lentiviral vector transduction techniques with murine adipose tissue-derived stem/stromal cells (mADSCs) as a new...

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Détails bibliographiques
Auteurs principaux: Watanabe, Natsumi, Ohashi, Kazuo, Tatsumi, Kohei, Utoh, Rie, Shim, In Kyong, Kanegae, Kazuko, Kashiwakura, Yuji, Ohmori, Tsukasa, Sakata, Yoichi, Inoue, Makoto, Hasegawa, Mamoru, Okano, Teruo
Format: Artigo
Langue:Inglês
Publié: Mary Ann Liebert, Inc. 2013
Sujets:
Accès en ligne:https://ncbi.nlm.nih.gov/pmc/articles/PMC3609603/
https://ncbi.nlm.nih.gov/pubmed/23360488
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2012.162
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