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Identification of 11 Novel Homogentisate 1,2 Dioxygenase Variants in Alkaptonuria Patients and Establishment of a Novel LOVD-Based HGD Mutation Database

Enzymatic loss in alkaptonuria (AKU), an autosomal recessive disorder, is caused by mutations in the homogentisate 1,2 dioxygenase (HGD) gene, which decrease or completely inactivate the function of the HGD protein to metabolize homogentisic acid (HGA). AKU shows a very low prevalence (1:100,000–250...

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Библиографические подробности
Главные авторы: Zatkova, Andrea, Sedlackova, Tatiana, Radvansky, Jan, Polakova, Helena, Nemethova, Martina, Aquaron, Robert, Dursun, Ismail, Usher, Jeannette L., Kadasi, Ludevit
Формат: Artigo
Язык:Inglês
Опубликовано: Springer Berlin Heidelberg 2011
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Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC3509877/
https://ncbi.nlm.nih.gov/pubmed/23430897
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2011_68
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