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Spinocerebellar ataxia type 13 mutation that is associated with disease onset in infancy disrupts axonal pathfinding during neuronal development

Spinocerebellar ataxia type 13 (SCA13) is an autosomal dominant disease caused by mutations in the Kv3.3 voltage-gated potassium (K(+)) channel. SCA13 exists in two forms: infant onset is characterized by severe cerebellar atrophy, persistent motor deficits and intellectual disability, whereas adult...

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Detalhes bibliográficos
Main Authors: Issa, Fadi A., Mock, Allan F., Sagasti, Alvaro, Papazian, Diane M.
Formato: Artigo
Idioma:Inglês
Publicado em: The Company of Biologists Limited 2012
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC3484873/
https://ncbi.nlm.nih.gov/pubmed/22736459
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1242/dmm.010157
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