Cargando...

Gene Therapy Approaches for Lysosomal Storage Disease: Next-Generation Treatment

Lysosomal storage diseases are a group of rare inborn errors of metabolism resulting from deficiency in normal lysosomal function. These diseases are characterized by progressive accumulation of storage material within the lysosomes of affected cells, ultimately leading to cellular dysfunction. Mult...

Descrición completa

Gardado en:
Detalles Bibliográficos
Main Authors: Byrne, Barry J., Falk, Darin J., Clément, Nathalie, Mah, Cathryn S.
Formato: Artigo
Idioma:Inglês
Publicado: Mary Ann Liebert, Inc. 2012
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC3413894/
https://ncbi.nlm.nih.gov/pubmed/22794786
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2012.140
Tags: Engadir etiqueta
Sen Etiquetas, Sexa o primeiro en etiquetar este rexistro!