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No evidence for mevalonate shunting in moderately affected children with Smith-Lemli-Opitz syndrome

Smith-Lemli-Opitz syndrome (SLOS) is caused by a genetic deficiency in 7-dehydrocholesterol (7-DHC) reductase (EC 1.3.1.21), the last enzyme of the cholesterol synthetic pathway. In SLOS, plasma cholesterol concentration is reduced and immediate precursor concentration (7-DHC) is elevated. Surprisin...

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Detalhes bibliográficos
Main Authors: Roullet, Jean-Baptiste, Merkens, Louise S., Pappu, Anurhada S., Jacob, Megan D., Winter, Rolf, Connor, William E., Steiner, Robert D.
Formato: Artigo
Idioma:Inglês
Publicado em: 2012
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC3404269/
https://ncbi.nlm.nih.gov/pubmed/22391996
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s10545-012-9453-6
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