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Progenitor Cell–Based Treatment of the Pediatric Myelin Disorders
The childhood leukodystrophies are characterized by neonatal or childhood deficiencies in myelin production or maintenance; these may be due to hereditary defects in genes for myelin maintenance, as in Pelizaeus-Merzbacher disease, or to enzymatic deficiencies resulting in substrate misaccumulation...
Kaydedildi:
| Yazar: | |
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| Materyal Türü: | Artigo |
| Dil: | Inglês |
| Baskı/Yayın Bilgisi: |
2011
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| Konular: | |
| Online Erişim: | https://ncbi.nlm.nih.gov/pmc/articles/PMC3358919/ https://ncbi.nlm.nih.gov/pubmed/21403006 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1001/archneurol.2011.46 |
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