Development of a disease severity scoring system for patients with Pompe disease

Ítems similars

• The Pompe Registry: tracking Pompe disease symptoms in a broad patient population
  per: Byrne, B, et al.
  Publicat: (2008)
• Antibody formation to enzyme therapy in classic infantile Pompe disease: implications of patient age
  per: van Gelder, C, et al.
  Publicat: (2013)
• Impact of enzyme replacement therapy on survival in adults with Pompe disease
  per: Güngör, Deniz, et al.
  Publicat: (2013)
• Enzyme replacement therapy and fatigue in adults with Pompe disease
  per: Güngör, Deniz, et al.
  Publicat: (2013)
• A higher dose of enzyme therapy in patients with classic infantile Pompe disease seems to improve ventilator-free survival and motor function
  per: van Gelder, C, et al.
  Publicat: (2013)