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Hematopoietic Stem Cell Transplantation in Thalassemia and Sickle Cell Anemia

The globally widespread single-gene disorders β-thalassemia and sickle cell anemia (SCA) can only be cured by allogeneic hematopoietic stem cell transplantation (HSCT). HSCT treatment of thalassemia has substantially improved over the last two decades, with advancements in preventive strategies, con...

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Autori principali: Lucarelli, Guido, Isgrò, Antonella, Sodani, Pietro, Gaziev, Javid
Natura: Artigo
Lingua:Inglês
Pubblicazione: Cold Spring Harbor Laboratory Press 2012
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC3331690/
https://ncbi.nlm.nih.gov/pubmed/22553502
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1101/cshperspect.a011825
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