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Sarcoglycanopathies: molecular pathogenesis and therapeutic prospects

Sarcoglycanopathies are a group of autosomal recessive muscle-wasting disorders caused by genetic defects in one of four cell membrane glycoproteins, α-, β-, γ- or δ-sarcoglycan. These four sarcoglycans form a subcomplex that is closely linked to the major dystrophin-associated protein complex, whic...

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Detalhes bibliográficos
Main Authors: Sandonà, Dorianna, Betto, Romeo
Formato: Artigo
Idioma:Inglês
Publicado em: Cambridge University Press 2009
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC3279956/
https://ncbi.nlm.nih.gov/pubmed/19781108
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1017/S1462399409001203
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