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Refsum's disease: characterization of the enzyme defect in cell culture

Refsum's disease (heredopathia atactica polyneuritiformis, HAP) is an inherited neurological disorder associated with storage of the branched-chain fatty acid, phytanic acid (3,7,11,15-tetramethylhexadecanoic acid). Cultured fibroblasts derived from skin biopsies of HAP patients did not contain...

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Detalles Bibliográficos
Main Authors: Herndon, James H., Steinberg, Daniel, Uhlendorf, B. William, Fales, Henry M.
Formato: Artigo
Idioma:Inglês
Publicado: 1969
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC322316/
https://ncbi.nlm.nih.gov/pubmed/4181593
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