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AAV8-mediated Hepatic Gene Transfer in Infant Rhesus Monkeys (Macaca mulatta)

Many genetic metabolic diseases manifest in infancy, therefore, it is important to develop effective treatments that could be implemented at this time. Adeno-associated virus serotype 8 (AAV8) gene transfer has been studied in neonatal mouse, cat, and dog models and shown some efficacy with a single...

Täydet tiedot

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Bibliografiset tiedot
Päätekijät: Wang, Lili, Bell, Peter, Lin, Jianping, Calcedo, Roberto, Tarantal, Alice F, Wilson, James M
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: Nature Publishing Group 2011
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC3222523/
https://ncbi.nlm.nih.gov/pubmed/21811248
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2011.151
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