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Cyclosporine A in Ullrich Congenital Muscular Dystrophy: Long-Term Results

Six individuals with Ullrich congenital muscular dystrophy (UCMD) and mutations in the genes-encoding collagen VI, aging 5–9, received 3–5 mg/kg of cyclosporine A (CsA) daily for 1 to 3.2 years. The primary outcome measure was the muscle strength evaluated with a myometer and expressed as megalimbs....

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Main Authors: Merlini, Luciano, Sabatelli, Patrizia, Armaroli, Annarita, Gnudi, Saverio, Angelin, Alessia, Grumati, Paolo, Michelini, Maria Elena, Franchella, Andrea, Gualandi, Francesca, Bertini, Enrico, Maraldi, Nadir Mario, Ferlini, Alessandra, Bonaldo, Paolo, Bernardi, Paolo
Formato: Artigo
Idioma:Inglês
Publicado: Hindawi Publishing Corporation 2011
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC3199070/
https://ncbi.nlm.nih.gov/pubmed/22028947
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1155/2011/139194
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