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The common missense mutation D489N in TRIM32 causing limb girdle muscular dystrophy 2H leads to loss of the mutated protein in knock-in mice resulting in a Trim32-null phenotype

Mutations in tripartite motif protein 32 (TRIM32) are responsible for several hereditary disorders that include limb girdle muscular dystrophy type 2H (LGMD2H), sarcotubular myopathy (STM) and Bardet Biedl syndrome. Most LGMD2H mutations in TRIM32 are clustered in the NHL β-propeller domain at the C...

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Main Authors: Kudryashova, Elena, Struyk, Arie, Mokhonova, Ekaterina, Cannon, Stephen C., Spencer, Melissa J.
Formato: Artigo
Idioma:Inglês
Publicado: Oxford University Press 2011
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Acceso en liña:https://ncbi.nlm.nih.gov/pmc/articles/PMC3177646/
https://ncbi.nlm.nih.gov/pubmed/21775502
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddr311
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