Stem Cell Gene Therapy for Fanconi Anemia: Report from the 1st International Fanconi Anemia Gene Therapy Working Group Meeting

Survival rates after allogeneic hematopoietic cell transplantation (HCT) for Fanconi anemia (FA) have increased dramatically since 2000. However, the use of autologous stem cell gene therapy, whereby the patient's own blood stem cells are modified to express the wild-type gene product, could po...

Descripció completa

Guardat en:
Dades bibliogràfiques
Autors principals: Tolar, Jakub, Adair, Jennifer E, Antoniou, Michael, Bartholomae, Cynthia C, Becker, Pamela S, Blazar, Bruce R, Bueren, Juan, Carroll, Thomas, Cavazzana-Calvo, Marina, Clapp, D Wade, Dalgleish, Robert, Galy, Anne, Gaspar, H Bobby, Hanenberg, Helmut, Von Kalle, Christof, Kiem, Hans-Peter, Lindeman, Dirk, Naldini, Luigi, Navarro, Susana, Renella, Raffaele, Rio, Paula, Sevilla, Julián, Schmidt, Manfred, Verhoeyen, Els, Wagner, John E, Williams, David A, Thrasher, Adrian J
Format: Artigo
Idioma:Inglês
Publicat: Nature Publishing Group 2011
Matèries:
Review
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC3129570/
https://ncbi.nlm.nih.gov/pubmed/21540837
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2011.78
Etiquetes: Afegir etiqueta
Sense etiquetes, Sigues el primer a etiquetar aquest registre!

Ítems similars