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Transport of Arylsulfatase A across the Blood-Brain Barrier in Vitro

Enzyme replacement therapy is an option to treat lysosomal storage diseases caused by functional deficiencies of lysosomal hydrolases as intravenous injection of therapeutic enzymes can correct the catabolic defect within many organ systems. However, beneficial effects on central nervous system mani...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Egile Nagusiak: Matthes, Frank, Wölte, Philipp, Böckenhoff, Annika, Hüwel, Sabine, Schulz, Mareike, Hyden, Pia, Fogh, Jens, Gieselmann, Volkmar, Galla, Hans-Joachim, Matzner, Ulrich
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: American Society for Biochemistry and Molecular Biology 2011
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC3093822/
https://ncbi.nlm.nih.gov/pubmed/21454621
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1074/jbc.M110.189381
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