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Adeno-associated viral vector-mediated gene transfer results in long-term enzymatic and functional correction in multiple organs of Fabry mice

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Detalles Bibliográficos
Publicado en:Proc Natl Acad Sci U S A
Main Authors: Jung, Sung-Chul, Han, Ina P., Limaye, Advait, Xu, Ruian, Gelderman, Monique P., Zerfas, Patricia, Tirumalai, Kamala, Murray, Gary J., During, Matthew J., Brady, Roscoe O., Qasba, Pankaj
Formato: Artigo
Idioma:Inglês
Publicado: National Academy of Sciences 2001
Assuntos:
Acceso en liña:https://ncbi.nlm.nih.govhttps://pmc.ncbi.nlm.nih.gov/articles/PMC30197/
https://ncbi.nlm.nih.govhttps://pubmed.ncbi.nlm.nih.gov/11226298/
https://ncbi.nlm.nih.govhttps://doi.org/10.1073/pnas.051634498
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