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Fabry Disease – Current Treatment and New Drug Development

Fabry disease is a rare inherited lysosomal storage disorder caused by a partial or complete deficiency of α-galactosidase A (GLA), resulting in the storage of excess cellular glycosphingolipids. Enzyme replacement therapy is available for the treatment of Fabry disease, but it is a costly, intraven...

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Bibliografiske detaljer
Main Authors: Motabar, Omid, Sidransky, Ellen, Goldin, Ehud, Zheng, Wei
Format: Artigo
Sprog:Inglês
Udgivet: Bentham Open 2010
Fag:
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC2995157/
https://ncbi.nlm.nih.gov/pubmed/21127742
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.2174/1875397301004010050
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