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Common and Uncommon Pathogenic Cascades in Lysosomal Storage Diseases

Lysosomal storage diseases (LSDs), of which about 50 are known, are caused by the defective activity of lysosomal proteins, resulting in accumulation of unmetabolized substrates. As a result, a variety of pathogenic cascades are activated such as altered calcium homeostasis, oxidative stress, inflam...

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Autori principali: Vitner, Einat B., Platt, Frances M., Futerman, Anthony H.
Natura: Artigo
Lingua:Inglês
Pubblicazione: American Society for Biochemistry and Molecular Biology 2010
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC2898325/
https://ncbi.nlm.nih.gov/pubmed/20430897
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1074/jbc.R110.134452
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