Peripheral transvenular delivery of adeno-associated viral vectors to skeletal muscle as a novel therapy for hemophilia B

Podobne zapisy

• Safety of AAV Factor IX Peripheral Transvenular Gene Delivery to Muscle in Hemophilia B Dogs
  od: Haurigot, Virginia, i wsp.
  Wydane: (2010)
• Translational Data from Adeno-Associated Virus-Mediated Gene Therapy of Hemophilia B in Dogs
  od: Nichols, Timothy C., i wsp.
  Wydane: (2015)
• Safety and efficacy of factor IX gene transfer to skeletal muscle in murine and canine hemophilia B models by adeno-associated viral vector serotype 1
  od: Arruda, Valder R., i wsp.
  Wydane: (2003)
• Protein Replacement Therapy and Gene Transfer in Canine Models of Hemophilia A, Hemophilia B, von Willebrand Disease, and Factor VII Deficiency
  od: Nichols, Timothy C., i wsp.
  Wydane: (2009)
• Regional intravascular delivery of AAV-2-F.IX to skeletal muscle achieves long-term correction of hemophilia B in a large animal model
  od: Arruda, Valder R., i wsp.
  Wydane: (2005)