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Nervous system and Fabry disease, from symptoms to diagnosis: damage evaluation and follow-up in adult patients, enzyme replacement, and support therapy

The X-linked genetic Fabry disease causes multiorgan lesions due to intracellular storage of the substrate globotriaosylceramide. Neurological involvement ranges from painful, small fiber neuropathy to cerebrovascular disorders to multifocal aggressive forms. Disease identification through proper di...

Täydet tiedot

Tallennettuna:
Bibliografiset tiedot
Päätekijät: Salviati, Alessandro, Burlina, Alessandro P., Borsini, Walter
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: Springer Milan 2010
Aiheet:
Linkit:https://ncbi.nlm.nih.gov/pmc/articles/PMC2869001/
https://ncbi.nlm.nih.gov/pubmed/20300794
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s10072-009-0211-y
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