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Long-term improvement in mdx cardiomyopathy after therapy with peptide-conjugated morpholino oligomers†

AIMS: The cardiomyopathy found in Duchenne muscular dystrophy (DMD) is responsible for death due to heart failure in ∼30% of patients and additionally contributes to many DMD morbidities. Strategies to bypass DMD-causing mutations to allow an increase in body-wide dystrophin have proved promising, b...

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Autors principals: Jearawiriyapaisarn, Natee, Moulton, Hong M., Sazani, Peter, Kole, Ryszard, Willis, Monte S.
Format: Artigo
Idioma:Inglês
Publicat: Oxford University Press 2010
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC2802205/
https://ncbi.nlm.nih.gov/pubmed/19815563
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/cvr/cvp335
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