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Allele dependent silencing of COL1A2 using small interfering RNAs

Osteogenesis imperfecta (OI) is generally caused by a dominant mutation in Collagen I, encoded by the genes COL1A1 and COL1A2. To date there is no satisfactory therapy for OI, but inactivation of the mutant allele through small interfering RNAs (siRNA) is a promising approach, as siRNAs targeting ea...

Ausführliche Beschreibung

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Bibliographische Detailangaben
Hauptverfasser: Lindahl, Katarina, Rubin, Carl-Johan, Kindmark, Andreas, Ljunggren, Östen
Format: Artigo
Sprache:Inglês
Veröffentlicht: Ivyspring International Publisher 2008
Schlagworte:
Online Zugang:https://ncbi.nlm.nih.gov/pmc/articles/PMC2583335/
https://ncbi.nlm.nih.gov/pubmed/19015742
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