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An Inducible Mouse Model for Epidermolysis Bullosa Simplex: Implications for Gene Therapy

The Dowling-Meara variant of epidermolysis bullosa simplex (EBS-DM) is a severe blistering disease inherited in an autosomal-dominant fashion. Here we report the generation of a mouse model that allows focal activation of a mutant keratin 14 allele in epidermal stem cells upon topical administration...

Deskribapen osoa

Gorde:
Xehetasun bibliografikoak
Egile Nagusiak: Cao, Tongyu, Longley, Mary Ann, Wang, Xiao-Jing, Roop, Dennis R.
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: The Rockefeller University Press 2001
Gaiak:
Sarrera elektronikoa:https://ncbi.nlm.nih.gov/pmc/articles/PMC2195993/
https://ncbi.nlm.nih.gov/pubmed/11157990
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