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Need to improve clinical trials in rare neurodegenerative disorders

Rare neurodegenerative diseases are fatal and no therapy is available to cure or slow down the progression of disease. We report possibly weaknesses in the management of clinical studies in these diseases, ranging from poor preclinical studies, difficulties in the recruitment of patients, delay in t...

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Gorde:
Xehetasun bibliografikoak
Egile Nagusiak: Maria Puopolo, Maurizio Pocchiari
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: Istituto Superiore di Sanità 2011-01-01
Saila:Annali dell'Istituto Superiore di Sanità
Gaiak:
Sarrera elektronikoa:http://www.scielosp.org/scielo.php?script=sci_arttext&pid=S0021-25712011000100012&lng=en&tlng=en
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