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Sebetralstat for On‐Demand Treatment of Mucosal Hereditary Angioedema Attacks in KONFIDENT‐S

ABSTRACT Background Hereditary angioedema (HAE‐C1INH) attacks involving mucosal tissue may progress rapidly and often lead to substantial morbidity. Severe laryngeal attacks can be fatal without prompt administration of on‐demand treatment. This prespecified interim analysis evaluated the safety and...

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Autori principali: Jonathan A. Bernstein, Emel Aygören‐Pürsün, Mauro Cancian, Danny M. Cohn, Timothy Craig, Vesna Grivcheva‐Panovska, Anthony Jordan, William R. Lumry, Inmaculada Martinez‐Saguer, Isaac Melamed, Kazumasa Ohmura, Jonny Peter, Marc A. Riedl, Daniel F. Soteres, Petra Staubach, Marcin Stobiecki, Ya‐Hsiu Chuang, Michael D. Smith, Christopher M. Yea, Paul K. Audhya, Andrea Zanichelli, Henriette Farkas
Natura: Artigo
Lingua:Inglês
Pubblicazione: Wiley 2025-11-01
Serie:Clinical and Translational Allergy
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Accesso online:https://doi.org/10.1002/clt2.70118
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