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Assessing brodalumab in the treatment of primary sclerosing cholangitis (SABR-PSC pilot study): protocol for a single-arm, multicentre, pilot study

Introduction Primary sclerosing cholangitis (PSC) is a rare immune-mediated hepatobiliary disease, characterised by progressive biliary fibrosis, cirrhosis, and end-stage liver disease. As yet, no licensed pharmacological therapy exists. While significant advancements have been made in our understan...

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Detalhes bibliográficos
Main Authors: Lee Shepstone, Emma Culver, Martine Walmsley, Douglas Thorburn, Palak Trivedi, Guruprasad Aithal, Jessica Dyson, Juliet High, Simon Rushbrook, Matthew Hammond, Leo Alexandre, Martin Pond, Amera Elzubeir
Formato: Artigo
Idioma:Inglês
Publicado em: BMJ Publishing Group 2025-07-01
Colecção:BMJ Open Gastroenterology
Acesso em linha:https://bmjopengastro.bmj.com/content/12/1/e001596.full
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