Gene therapy in the putamen for curing AADC deficiency and Parkinson's disease

Abstract This commentary provides an overview of the putamen as an established target site for gene therapy in treating aromatic l‐amino acid decarboxylase (AADC) deficiency and Parkinson’s disease, two debilitating neurological disorders that involve motor dysfunction caused by dopamine deficiencie...

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Auteurs principaux:	Paul Wuh‐Liang Hwu, Karl Kiening, Irina Anselm, David R Compton, Takeshi Nakajima, Thomas Opladen, Phillip L Pearl, Agathe Roubertie, Thomas Roujeau, Shin‐ichi Muramatsu
Format:	Artigo
Langue:	Inglês
Publié:	Springer Nature 2021-08-01
Collection:	EMBO Molecular Medicine
Sujets:	AADC deficiency aromatic l‐amino acid decarboxylase dopamine gene therapy putamen
Accès en ligne:	https://doi.org/10.15252/emmm.202114712
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