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Current Drug Repurposing Strategies for Rare Neurodegenerative Disorders

Rare diseases are life-threatening or chronically debilitating low-prevalent disorders caused by pathogenic mutations or particular environmental insults. Due to their high complexity and low frequency, important gaps still exist in their prevention, diagnosis, and treatment. Since new drug discover...

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Autores principales: Sweta Shah, Marc Marie Dooms, Sofia Amaral-Garcia, Mariana Igoillo-Esteve
Formato: Artigo
Lenguaje:Inglês
Publicado: Frontiers Media S.A. 2021-12-01
Colección:Frontiers in Pharmacology
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Acceso en línea:https://www.frontiersin.org/articles/10.3389/fphar.2021.768023/full
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