Remaining Burden of Spinal Muscular Atrophy Among Treated Patients: A Survey of Patients and Caregivers

ABSTRACT Objective Spinal muscular atrophy (SMA) significantly impacts motor function. This study aimed to assess the persistent burden and unmet needs among currently treated patients with SMA and their caregivers. Methods Two complementary web‐based surveys were distributed in August 2024 among pa...

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Detalles Bibliográficos

Autores principales:	Julie A. Parsons, Natalie Land, Melissa Culhane Maravic, Claire Cagle, Amal Jamaleddine, Hemal Shah, Thomas Brown, Christabella Cherubino, Mouhamed Gueye
Formato:	Artigo
Lenguaje:	Inglês
Publicado:	Wiley 2025-10-01
Colección:	Annals of Clinical and Translational Neurology
Materias:	disease burden fatigue muscle weakness spinal muscular atrophy unmet need
Acceso en línea:	https://doi.org/10.1002/acn3.70132
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