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Assessing thrombogenesis and treatment response in congenital thrombotic thrombocytopenic purpura

Abstract Despite clinical remission and normal platelet counts, congenital TTP (cTTP) is associated with non‐overt symptoms. Prophylactic ADAMTS13 replacement therapy such as plasma infusion (PI) prevents acute episodes and improves symptomatology. There is no current method to investigate disease s...

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Autori principali: Ferras Alwan, Chiara Vendramin, Ulrich Budde, Ri Liesner, Alice Taylor, Mari Thomas, Bernhard Lämmle, Marie Scully
Natura: Artigo
Lingua:Inglês
Pubblicazione: Wiley 2021-05-01
Serie:eJHaem
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Accesso online:https://doi.org/10.1002/jha2.178
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