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Evaluating the long-term benefits of hydroxyurea in pediatric sickle cell anemia

Abstract: Hydroxyurea is the primary disease-modifying medication for sickle cell anemia (SCA), but its long-term effects, particularly how these effects change over time, are not well understood. This study aimed to quantify the effects of hydroxyurea on clinical and laboratory outcomes in children...

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Principais autores: Paul George, Grace Kalmus, Peter A. Lane, Wilbur Lam, Joseph Lipscomb, David Howard
Formato: Artigo
Idioma:Inglês
Publicado: Elsevier 2025-07-01
Series:Blood Advances
Acceso en liña:http://www.sciencedirect.com/science/article/pii/S247395292500237X
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