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P338: Objectives and design of the Acorn Study: A non-interventional study evaluating long-term safety in achondroplasia patients treated with vosoritide

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書目詳細資料
Principais autores: Jeanne Pimenta, Shelda Cohen, Swati Mukherjee, Fiona Fettes, Kala Jayaram, Ekkehart Lausch
格式: Artigo
語言:Inglês
出版: Elsevier 2023-01-01
叢編:Genetics in Medicine Open
在線閱讀:http://www.sciencedirect.com/science/article/pii/S2949774423003667
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