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Oral and Swallowing Abilities Tool (OrSAT) in Individuals with Type I SMA Older than 24 Months: A Pilot Study

<b>Background/Objectives</b>: The advent of disease modifying therapies (DMTs) for Spinal Muscular Atrophy (SMA) has highlighted the need for reliable tools to assess bulbar function in type I individuals. The Oral and Swallowing Abilities Tool (OrSAT) was originally developed to evaluate swallowing...

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Bibliografiske detaljer
Principais autores: Giulia Stanca, Maria Sframeli, Camilla Verdilio, Beatrice Berti, Lavinia Fanelli, Natalia Longoni, Marisa Maniaci, Giorgia Coratti, Chiara Cutrì, Roberta Onesimo, Concetta Palermo, Daniela Leone, Anna Falco, Giulia Norcia, Valentina Giorgio, Carolina Ausili Cefaro, Antonella Cerchiari, Sonia Messina, Marika Pane, Eugenio Mercuri
Format: Artigo
Sprog:Inglês
Udgivet: MDPI AG 2026-06-01
Serier:Children
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Online adgang:https://www.mdpi.com/2227-9067/13/6/773
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