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Aptamer–ODN Chimeras: Enabling Cell-Specific ODN Targeting Therapy

Oligonucleotides (ODNs) such as siRNA, saRNA, and miRNA regulate gene expression through a variety of molecular mechanisms and show unique potential in the treatment of genetic diseases and rare diseases, but their clinical application is still limited by the efficiency of the delivery system, espec...

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Autori principali: Bei Xia, Qubo Zhu
Natura: Artigo
Lingua:Inglês
Pubblicazione: MDPI AG 2025-05-01
Serie:Cells
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Accesso online:https://www.mdpi.com/2073-4409/14/10/697
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