Código QR

SNA-modified antisense oligonucleotides: A new pathway for renal targeting?

Antisense oligonucleotides (ASOs) have emerged as a powerful class of therapeutics capable of suppressing gene expression with remarkable specificity. However, the clinical applications of ASOs have been limited by delivery challenges and toxicities, particularly when repeated or high dosing is requ...

Descripción completa

Guardado en:
Detalles Bibliográficos
Autores principales: Bernhard Dumoulin, Ken Yamada, Katalin Susztak
Formato: Artigo
Lenguaje:Inglês
Publicado: Elsevier 2025-03-01
Colección:Molecular Therapy: Nucleic Acids
Acceso en línea:http://www.sciencedirect.com/science/article/pii/S2162253125000307
Etiquetas: Agregar Etiqueta
Sin Etiquetas, Sea el primero en etiquetar este registro!