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Novel Gene-Correction-Based Therapeutic Modalities for Monogenic Liver Disorders

The majority of monogenic liver diseases are autosomal recessive disorders, with few being sex-related or co-dominant. Although orthotopic liver transplantation (LT) is currently the sole therapeutic option for end-stage patients, such an invasive surgical approach is severely restricted by the lack...

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-д хадгалсан:
Номзүйн дэлгэрэнгүй
Үндсэн зохиолчид: Mahsa Ghasemzad, Mahdieh Hashemi, Zohre Miri Lavasani, Nikoo Hossein-khannazer, Haleh Bakhshandeh, Roberto Gramignoli, Hani Keshavarz Alikhani, Mustapha Najimi, Saman Nikeghbalian, Massoud Vosough
Формат: Artigo
Хэл сонгох:Inglês
Хэвлэсэн: MDPI AG 2022-08-01
Цуврал:Bioengineering
Нөхцлүүд:
Онлайн хандалт:https://www.mdpi.com/2306-5354/9/8/392
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