Long-term outcomes with agalsidase alfa enzyme replacement therapy: Analysis using deconstructed composite events
This is a retrospective analysis of Fabry Outcome Survey data from children/adults (n = 677) receiving agalsidase alfa enzyme replacement therapy for a median of 3 years, examining cerebrovascular, cardiac, and renal morbidity endpoints separately. Cardiac events occurred at younger ages than cerebr...
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| Главные авторы: | , , , , , , |
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| Формат: | Artigo |
| Язык: | Inglês |
| Опубликовано: |
Elsevier
2018-03-01
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| Серии: | Molecular Genetics and Metabolism Reports |
| Предметы: | |
| Online-ссылка: | http://www.sciencedirect.com/science/article/pii/S2214426917301039 |
| Метки: |
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