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Current Status and Prospects of Gene Therapy for Primary Ciliary Dyskinesia

Primary ciliary dyskinesia (PCD) is a genetically heterogeneous disease characterized by structural or functional abnormalities of motile cilia. It often presents clinically with recurrent respiratory infections, situs inversus, hydrocephalus, and infertility. Currently, there is no clinical treatme...

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Detaylı Bibliyografya
Asıl Yazarlar: LU Wanqing, LI Yixuan, HE Miao, TIAN Xinlun, LIU Yaping
Materyal Türü: Artigo
Dil:Chinês
Baskı/Yayın Bilgisi: Editorial Office of Journal of Rare Diseases 2025-07-01
Seri Bilgileri:罕见病研究
Konular:
Online Erişim:https://jrd.chard.org.cn/article/doi/10.12376/j.issn.2097-0501.2025.03.015
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