Current Status and Prospects of Gene Therapy for Primary Ciliary Dyskinesia
Primary ciliary dyskinesia (PCD) is a genetically heterogeneous disease characterized by structural or functional abnormalities of motile cilia. It often presents clinically with recurrent respiratory infections, situs inversus, hydrocephalus, and infertility. Currently, there is no clinical treatme...
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| Asıl Yazarlar: | , , , , |
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| Materyal Türü: | Artigo |
| Dil: | Chinês |
| Baskı/Yayın Bilgisi: |
Editorial Office of Journal of Rare Diseases
2025-07-01
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| Seri Bilgileri: | 罕见病研究 |
| Konular: | |
| Online Erişim: | https://jrd.chard.org.cn/article/doi/10.12376/j.issn.2097-0501.2025.03.015 |
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