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Educational attainment of individuals with lymphangioleiomyomatosis is a determinant of timely diagnosis and treatment uptake

Abstract Background Lymphangioleiomyomatosis (LAM) is a rare, progressive lung disease predominantly affecting women. Despite the availability of FDA-approved treatments, mTOR inhibitors like sirolimus or everolimus, significant disparities persist in early diagnosis, treatment utilization, and pati...

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Hlavní autor: Marina K. Holz
Médium: Artigo
Jazyk:Inglês
Vydáno: BMC 2026-02-01
Edice:Orphanet Journal of Rare Diseases
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On-line přístup:https://doi.org/10.1186/s13023-026-04284-8
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