Stem cell and gene therapies for leukodystrophies
Leukodystrophies form a group of rare genetic disorders characterized by the progressive degeneration of white matter in the brain, often presenting in childhood with life-threatening consequences. Current therapeutic options are limited, particularly after symptom onset, and delayed diagnosis exace...
Guardat en:
| Autors principals: | , , , |
|---|---|
| Format: | Artigo |
| Idioma: | Inglês |
| Publicat: |
Elsevier
2025-09-01
|
| Col·lecció: | Molecular Therapy: Methods & Clinical Development |
| Matèries: | |
| Accés en línia: | http://www.sciencedirect.com/science/article/pii/S2329050125001226 |
| Etiquetes: |
Sense etiquetes, Sigues el primer a etiquetar aquest registre!
|