Emerging Therapeutic Approaches for Cystic Fibrosis. From Gene Editing to Personalized Medicine

An improved understanding of the cystic fibrosis (CF) transmembrane conductance regulator (CFTR) protein structure and the consequences of CFTR gene mutations have allowed the development of novel therapies targeting specific defects underlying CF. Some strategies are mutation specific and have alre...

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Номзүйн дэлгэрэнгүй

Үндсэн зохиолчид:	Iwona Pranke, Anita Golec, Alexandre Hinzpeter, Aleksander Edelman, Isabelle Sermet-Gaudelus
Формат:	Artigo
Хэл сонгох:	Inglês
Хэвлэсэн:	Frontiers Media S.A. 2019-02-01
Цуврал:	Frontiers in Pharmacology
Нөхцлүүд:	cystic fibrosis CFTR ivacaftor CFTR modulator gene therapy
Онлайн хандалт:	https://www.frontiersin.org/article/10.3389/fphar.2019.00121/full
Шошгууд:	Шошго нэмэх Шошго байхгүй, Энэхүү баримтыг шошголох эхний хүн болох!