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Development of a core outcome set for paediatric achalasia: a joint ERNICA, ESPGHAN and EUPSA study protocol

Introduction Achalasia is a rare disease in children. Studies investigating the efficacy of interventions and disease outcomes in paediatric achalasia are predominantly retrospective, consist of small cohorts and report heterogeneous outcomes. The variation in the use and definition of reported outc...

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Principais autores: Simon Eaton, Nigel J Hall, Frederic Gottrand, Jonathan J Neville, Iris den Uijl, Willemijn Irvine
Formato: Artigo
Idioma:Inglês
Publicado em: BMJ Publishing Group 2025-02-01
coleção:BMJ Paediatrics Open
Acesso em linha:https://bmjpaedsopen.bmj.com/content/9/1/e003130.full
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