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Homozygous slc25a20 zebrafish mutant reveals insights into carnitine-acylcarnitine translocase deficiency pathogenesis

The SLC25A20 gene encodes carnitine-acylcarnitine translocase (CACT), facilitating the transport of long-chain acylcarnitine required for energy production via β-oxidation into the mitochondria. Loss-of-function mutations in this gene lead to CACT deficiency, a rare autosomal recessive disorder of f...

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Bibliografski detalji
Glavni autori: Ryuichi Hishida, Kohei Ishiguro, Tomoyuki Yamanaka, Shinya Toyokuni, Hideaki Matsui
Format: Artigo
Jezik:Inglês
Izdano: Elsevier 2024-12-01
Serija:Molecular Genetics and Metabolism Reports
Teme:
Online pristup:http://www.sciencedirect.com/science/article/pii/S2214426924001186
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