Código QR (código de barras bidimensional)

Evaluation of Mono- and Bi-Functional GLOBE-Based Vectors for Therapy of β-Thalassemia by <i>HBB<sup>AS3</sup></i> Gene Addition and Mutation-Specific RNA Interference

Therapy via the gene addition of the anti-sickling β<sup>AS3</sup>-globin transgene is potentially curative for all β-hemoglobinopathies and therefore of particular clinical and commercial interest. This study investigates GLOBE-based lentiviral vectors (LVs) for β<sup>AS3</sup>-globin addition and...

ver descrição completa

Na minha lista:
Principais autores: Lola Koniali, Christina Flouri, Markela I. Kostopoulou, Nikoletta Y. Papaioannou, Panayiota L. Papasavva, Basma Naiisseh, Coralea Stephanou, Anthi Demetriadou, Maria Sitarou, Soteroula Christou, Michael N. Antoniou, Marina Kleanthous, Petros Patsali, Carsten W. Lederer
Formato: Artigo
Idioma:Inglês
Publicado em: MDPI AG 2023-12-01
coleção:Cells
Assuntos:
gene therapy
RNA interference
shRNAmiR
lentiviral vector
hemoglobinopathy
thalassemia
Acesso em linha:https://www.mdpi.com/2073-4409/12/24/2848
Tags: Adicionar Tag
Sem tags, seja o primeiro a adicionar uma tag!

Registros relacionados