Comparative efficacy and safety of olezarsen versus volanesorsen for familial chylomicronemia syndrome: a matching-adjusted indirect comparison

Background: Familial chylomicronemia syndrome (FCS) is a rare genetic disorder characterized by severe hypertriglyceridemia causing recurrent acute pancreatitis (AP). Since FCS is a genetic deficiency in functional lipoprotein lipase, conventional triglyceride-lowering therapies are ineffective in...

Бүрэн тодорхойлолт

Номзүйн дэлгэрэнгүй

Үндсэн зохиолчид:	Handrean Soran, Asia Sikora Kessler, Montserrat Vera-Llonch, Veronica J Alexander, Paul Serafini, Divya Pushkarna, Elisabete Rodrigues, Erik Stroes, Ulrike Schatz, Ursula Kassner, Zalmai Hakimi, Aletta Falk, Koo Wilson
Формат:	Artigo
Хэл сонгох:	Inglês
Хэвлэсэн:	Becaris Publishing Limited 2026-06-01
Цуврал:	Journal of Comparative Effectiveness Research
Нөхцлүүд:	familial chylomicronemia syndrome hypertriglyceridemia indirect treatment comparison olezarsen volanesorsen
Шошгууд:	Шошго нэмэх Шошго байхгүй, Энэхүү баримтыг шошголох эхний хүн болох!