Drug repurposing for rare: progress and opportunities for the rare disease community

Repurposing is one of the key opportunities to address the unmet rare diseases therapeutic need. Based on cases of drug repurposing in small population conditions, and previous work in drug repurposing, we analyzed the most important lessons learned, such as the sharing of clinical observations, rea...

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Bibliografske podrobnosti

Principais autores:	Anneliene Hechtelt Jonker, Daniel O’Connor, Maria Cavaller-Bellaubi, Christine Fetro, Maria Gogou, Peter A. C. ’T Hoen, Martin de Kort, Heather Stone, Nivedita Valentine, Anna Maria Gerdina Pasmooij
Format:	Artigo
Jezik:	Inglês
Izdano:	Frontiers Media S.A. 2024-01-01
Serija:	Frontiers in Medicine
Teme:	drug repurposing rare diseases orphan drugs unmet need innovation therapy development
Online dostop:	https://www.frontiersin.org/articles/10.3389/fmed.2024.1352803/full
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