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Symptom Changes in Pediatric Patients with Activated Phosphoinositide 3-Kinase Delta Syndrome (APDS) Receiving Leniolisib

IntroductionActivated Phosphoinositide 3-Kinase Delta Syndrome (APDS) is a rare disease characterized by progressive symptoms that begin early in life, including lymphoproliferation, recurrent and persistent infections, and early mortality compared with the global population. Delayed diagnosis and i...

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Principais autores: Rohith Jesudas, Chad Gwaltney, Leanne Stanley, Carrie R. Houts, Jason Bradt, Amanda Harrington
Formato: Artigo
Idioma:Inglês
Publicado em: Rockefeller University Press 2026-05-01
coleção:Journal of Human Immunity
Acesso em linha:https://rupress.org/jhi/article/2/CIS2026/eCIS2026abstract.105/281941/Symptom-Changes-in-Pediatric-Patients-with
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