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Long‐Term Clinical‐Pathologic Results of Enzyme Replacement Therapy in Prehypertrophic Fabry Disease Cardiomyopathy

Background The limited ability of enzyme replacement therapy (ERT) in removing globotriaosylceramide from cardiomyocytes is recognized for advanced Fabry disease cardiomyopathy (FDCM). Prehypertrophic FDCM is believed to be cured or stabilized by ERT. However, no pathologic confirmation is available...

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Збережено в:
Бібліографічні деталі
Автори: Andrea Frustaci, Romina Verardo, Nicola Galea, Maria Alfarano, Michele Magnocavallo, Livia Marchitelli, Luigi Sansone, Manuel Belli, Mario Cristina, Emanuela Frustaci, Matteo Antonio Russo, Cristina Chimenti
Формат: Artigo
Мова:Inglês
Опубліковано: Wiley 2024-04-01
Серія:Journal of the American Heart Association: Cardiovascular and Cerebrovascular Disease
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Онлайн доступ:https://www.ahajournals.org/doi/10.1161/JAHA.123.032734
Теги: Додати тег
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