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Effect of nusinersen on pulmonary function in children with spinal muscular atrophy in the plateau region: A pilot study

Background: The drug nusinersen is applied to improve motor function in patients with spinal muscle atrophy (SMA). However, research on the effects of this treatment on lung function is lacking. Aim: To investigate the effect of nusinersen on lung function in children with SMA in the Plateau. Method...

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Autors principals: Jicai Zhu, Xiaofang Chen, Haoke Sang, Minming Ma, Chunhui Tang
Format: Artigo
Idioma:Inglês
Publicat: Elsevier 2025-01-01
Col·lecció:Heliyon
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Accés en línia:http://www.sciencedirect.com/science/article/pii/S2405844024174191
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