Enzyme replacement therapy compared with best supportive care for the treatment of Pompe Disease: a systematic review and network meta-analysis

Background Late-onset Pompe disease is a rare inherited genetic condition that causes progressive muscle dysfunction and damage. As the disease advances, the progressive weakening of respiratory muscles significantly increases the risk of respiratory failure, which is a major contributor to prematur...

תיאור מלא

מידע ביבליוגרפי

Principais autores:	Mark Corbett, Chinyereugo Umemneku-Chikere, Sarah Nevitt, Nyanar Jasmine Deng, Matthew Walton, Helen Fulbright, Chong Yew Tan, Robin Lachmann, Rachel Churchill, Robert Hodgson
פורמט:	Artigo
שפה:	Inglês
יצא לאור:	NIHR Journals Library 2026-02-01
סדרה:	Health Technology Assessment
נושאים:	glycogen storage disease type ii enzyme replacement therapy network meta-analysis humans
גישה מקוונת:	https://doi.org/10.3310/GJRH0730
תגים:	הוספת תג אין תגיות, היה/י הראשונ/ה לתייג את הרשומה!